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    Rare Diseases Stocks List

    Symbol Grade Name % Change
    BLUE F bluebird bio, Inc. -1.68
    BOLD F Boundless Bio, Inc. -5.17
    RLYB F Rallybio Corporaton -0.55
    IONS F Ionis Pharmaceuticals, Inc. -4.12
    BMRN F BioMarin Pharmaceutical Inc. 1.42
    AZTR F Azitra Inc. 0.00
    CNTG F Centogene N.V. 0.00
    GSK F GlaxoSmithKline PLC 0.00
    NGNE F Neurogene, Inc. 1.70
    XFOR F X4 Pharmaceuticals, Inc. 8.23
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    Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
    Related Stock Lists: Epidermolysis Bullosa Genodermatoses Disease Medicine Biopharmaceutical Biotechnology Clinical Development Clinical Medicine Dermatology Life Sciences Medical Genetics Organ Systems Acid Acute Pain Aesthetics Amphetamine Angioedema Ataxia Attention Deficit Hyperactivity Disorder Bone

    Related ETFs - A few ETFs which own one or more of the above listed Rare Diseases stocks.

    Symbol Grade Name Weight
    PPH D Market Vectors Pharmaceutical ETF 4.6
    HRTS F Tema Cardiovascular and Metabolic ETF 3.81
    GINX D SGI Enhanced Global Income ETF 3.79
    GNOM F Global X Genomics & Biotechnology ETF 3.63
    BBC F Virtus LifeSci Biotech Clinical Trials ETF 2.99
    View all Rare Diseases ETFs...
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    Compare HRTS to GINX Compare PPH to BBC Compare PPH to HRTS

        Rare Diseases Stocks Recent News

        Date Stock Title
        Nov 21 BMRN Why Is BioMarin Pharmaceutical Inc. (BMRN) Among the Worst Performing Biotech Stocks in 2024?
        Nov 21 IONS Why Is Ionis Pharmaceuticals, Inc. (IONS) Among the Worst Performing Biotech Stocks in 2024?
        Nov 21 BMRN BioMarin: Challenges Mount, But Sale Rumors Make For A Risky 'Buy' Call
        Nov 21 BMRN Here's Why BioMarin Pharmaceutical (BMRN) is a Strong Value Stock
        Nov 20 GSK CDC warns of an imminent spike in COVID, flu cases
        Nov 20 XFOR Spotlight On 3 US Penny Stocks With At Least $60M Market Cap
        Nov 20 IONS Ionis Pharmaceuticals, Inc. (IONS): Among the Best Genomics Stocks to Buy Right Now
        Nov 19 BMRN BioMarin Pharmaceutical Inc. (BMRN): Among the Best Genomics Stocks to Buy Right Now
        Nov 19 GSK GSK's Investigational Liver Disease Candidate Hits Primary Goal In Late-Stage Study To Treat Relentless Itch In Some Patients
        Nov 19 GSK GSK's Investigational Liver Disease Candidate Hits Primary Goal In Late-Stage Study To Treat Relentless Itch In Some Patients
        Nov 19 GSK GSK reports positive Phase 3 results for linerixibat in PBC itching
        Nov 19 NGNE Neurogene GAAP EPS of -$1.19 in-line
        Nov 18 NGNE Neurogene Reports Third Quarter 2024 Financial Results and Highlights Recent Updates
        Nov 18 NGNE How A Side Effect Has Wiped Out 73% Of Neurogene's Value In A Week
        Nov 18 NGNE Neurogene stock plunges 36% on NGN-401 study update
        Nov 18 IONS Here's Why Ionis Pharmaceuticals (IONS) is Poised for a Turnaround After Losing -13.46% in 4 Weeks
        Nov 18 GSK Medicus Pharma Ltd. Appoints Faisal Mehmud, MD, MRCP as Chief Medical Officer
        Nov 18 NGNE Neurogene Provides Update on NGN-401 Gene Therapy Clinical Trial for Rett Syndrome
        Nov 16 BMRN BioMarin Presents Real-World Evidence Further Supporting Safety and Efficacy of VOXZOGO® (vosoritide) in Children with Achondroplasia at the European Society for Paediatric Endocrinology (ESPE) Meeting 2024
        Nov 16 BLUE bluebird bio Third Quarter 2024 Earnings: EPS Beats Expectations, Revenues Lag
        Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
        Related Stock Lists: Epidermolysis Bullosa Genodermatoses Disease Medicine Biopharmaceutical Biotechnology Clinical Development Clinical Medicine Dermatology Life Sciences Medical Genetics Organ Systems Acid Acute Pain Aesthetics Amphetamine Angioedema Ataxia Attention Deficit Hyperactivity Disorder Bone
        Rare Diseases

        Rare diseases are medical conditions that affect a small percentage of the population. They are often genetic, chronic, and progressive, and can cause significant physical and mental disability. There are over 7,000 rare diseases, and many of them have no known cure.

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