or Try an Advanced Search...

    Rare Diseases Stocks List

    Symbol Grade Name % Change
    INM F InMed Pharmaceuticals Inc. -8.30
    AKTX F Akari Therapeutics Plc -7.48
    PHVS D Pharvaris N.V. -3.95
    PULM C Pulmatrix, Inc. -3.44
    IONS F Ionis Pharmaceuticals, Inc. -2.60
    PASG D Passage Bio, Inc. -2.24
    BMRN F BioMarin Pharmaceutical Inc. -1.62
    ALDX C Aldeyra Therapeutics, Inc. -1.19
    RARE D Ultragenyx Pharmaceutical Inc. -1.04
    AVRO D AVROBIO, Inc. -0.81
    View As Page of Charts
    Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
    Related Stock Lists: Biopharmaceutical Medicine Cancer Organ Systems Biotechnology Dermatology Disease Drug Discovery Enzyme Replacement Therapy Epidermolysis Bullosa Genetics Genodermatoses Inborn Errors Of Metabolism Lysosomal Storage Disorder Ocular Disease Orphan Drug Pompe Disease Severe And Rare Diseases Achondroplasia Acquired Hemolytic Anemia

    Related ETFs - A few ETFs which own one or more of the above listed Rare Diseases stocks.

    Symbol Grade Name Weight
    GNOM D Global X Genomics & Biotechnology ETF 4.95
    TMFS B Motley Fool Small-Cap Growth ETF 2.98
    TMFM A Motley Fool Mid-Cap Growth ETF 2.09
    BBP D BioShares Biotechnology Products Fund 2.01
    LABD D Direxion Daily S&P Biotech Bear 3X Shares 1.49
    View all Rare Diseases ETFs...
    Compare ETFs
    Compare GNOM to BBP Compare GNOM to LABD Compare GNOM to TMFS

        Rare Diseases Stocks Recent News

        Date Stock Title
        May 3 RARE Ultragenyx Pharmaceutical Inc (RARE) (Q1 2024) Earnings Call Transcript Highlights: Key ...
        May 3 RARE Ultragenyx (RARE) Q1 Loss Wider Than Expected, Revenues Rise Y/Y
        May 3 RARE Ultragenyx Pharmaceutical, Inc. (RARE) Q1 2024 Earnings Call Transcript
        May 2 RARE Ultragenyx Pharmaceutical Inc (RARE) Q1 2024 Earnings: Misses EPS Estimates, Revenue Grows ...
        May 2 RARE Ultragenyx Pharmaceutical GAAP EPS of -$2.03 misses by $0.28, revenue of $108.8M misses by $7.64M
        May 2 RARE Ultragenyx Reports First Quarter 2024 Financial Results and Corporate Update
        May 1 RARE Ultragenyx Pharmaceutical Q1 2024 Earnings Preview
        May 1 AKTX Akari gains despite leadership change amid portfolio shakeup
        May 1 IONS 4D Molecular Therapeutics, Inc. (FDMT) May Report Negative Earnings: Know the Trend Ahead of Q1 Release
        May 1 AKTX Samir R. Patel, M.D. Appointed Interim CEO for Akari Therapeutics
        May 1 AKTX Akari Therapeutics and Peak Bio Announce Portfolio Prioritization Plan for Combined Go-Forward Merger Entity
        Apr 30 RARE Ultragenyx Issues 2023 Corporate Responsibility Report, Showcasing Commitment to Improving Equity and Access to Innovation in Rare Disease
        Apr 30 IONS Ionis Pharmaceuticals (IONS) Expected to Beat Earnings Estimates: What to Know Ahead of Q1 Release
        Apr 30 RARE Ultragenyx Announces Completion of Enrollment in Phase 3 Orbit and Cosmic Studies Evaluating Setrusumab (UX143) for the Treatment of Osteogenesis Imperfecta (OI)
        Apr 30 BMRN BioMarin Pharmaceutical Inc. Beat Analyst Estimates: See What The Consensus Is Forecasting For This Year
        Apr 29 BMRN BioMarin Pharmaceutical Investors Overfocused on Roctavian, Distracted From Enzyme Replacement Therapies, UBS Says
        Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
        Related Stock Lists: Biotechnology Life Sciences Biopharmaceutical Cancer Gene Therapy Organ Systems Central Nervous System Disorders Gene Delivery Lipid Storage Disorders Medicine Monogenic Anemia Applied Genetics Ataxia Biology Bone Bone Disease Clinical Development Clinical Pharmacology Deficiency
        Rare Diseases

        Rare diseases are medical conditions that affect a small percentage of the population. They are often genetic, chronic, and progressive, and can cause significant physical and mental disability. There are over 7,000 rare diseases, and many of them have no known cure.

        Browse All Tags