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    Rare Diseases Stocks List

    Symbol Grade Name % Change
    MREO B Mereo BioPharma Group plc 6.52
    KRYS B Krystal Biotech, Inc. -2.70
    TSHA B Taysha Gene Therapies, Inc. -4.80
    WVE B WAVE Life Sciences Ltd. -3.86
    NGNE B Neurogene, Inc. 1.43
    AKTX B Akari Therapeutics Plc 3.61
    AVRO B AVROBIO, Inc. -2.72
    LXEO C Lexeo Therapeutics, Inc. -7.36
    LRMR C Larimar Therapeutics, Inc. -3.10
    DNTH C Dianthus Therapeutics, Inc. -3.56
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    Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
    Related Stock Lists: Biotechnology Gene Therapy Medical Genetics Ataxia Biopharmaceutical Drug Discovery Epidermolysis Bullosa Friedreich's Ataxia Gene Delivery Genetic Diseases Genetic Engineering Genodermatoses Life Sciences Lipid Storage Disorders Medicine Acid Acquired Hemolytic Anemia Antibodies Antibody Applied Genetics

    Related ETFs - A few ETFs which own one or more of the above listed Rare Diseases stocks.

    Symbol Grade Name Weight
    PINK A Simplify Health Care ETF 12.66
    BBP B BioShares Biotechnology Products Fund 9.36
    PBE B PowerShares Dynamic Biotech & Genome 8.3
    IDNA B iShares Genomics Immunology and Healthcare ETF 7.53
    GNOM C Global X Genomics & Biotechnology ETF 6.99
    View all Rare Diseases ETFs...
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    Compare BBP to PBE Compare PINK to GNOM Compare PINK to IDNA

        Rare Diseases Stocks Recent News

        Date Stock Title
        Jun 14 MREO Mereo BioPharma Announces Pricing of $50 Million Underwritten Registered Direct Offering of American Depository Shares, Priced At-the-Market
        Jun 13 MREO Baird starts Mereo at outperform, sees alvelestat as underappreciated
        Jun 13 LXEO Companies Like Lexeo Therapeutics (NASDAQ:LXEO) Are In A Position To Invest In Growth
        Jun 12 MREO Ultragenyx (RARE) Posts New Data From Bone Disease Study
        Jun 12 MREO Mereo spikes after mid-stage data for Ultragenyx-partnered bone disorder therapy
        Jun 12 WVE Wave Life Sciences Announces Upcoming Presentations Highlighting Novel siRNA Program in Obesity and Leadership in RNA Editing
        Jun 12 DNTH Dianthus wins FDA nod to start mid-stage trial for lead asset
        Jun 12 MREO Ultragenyx, Mereo drug reduces fractures in bone disorder study
        Jun 12 TSHA Taysha Gene Therapies to Present Clinical Data from Both REVEAL Phase 1/2 Trials During Company-Hosted Webcast and at 2024 IRSF Rett Syndrome Scientific Meeting
        Jun 12 DNTH Dianthus Therapeutics Announces FDA Clearance to Initiate Phase 2 Trial of DNTH103 in Multifocal Motor Neuropathy (MMN)
        Jun 12 MREO Why Oracle Shares Are Trading Higher By 9%; Here Are 20 Stocks Moving Premarket
        Jun 11 MREO Ultragenyx and Mereo BioPharma Announce New Phase 2 Data from Phase 2/3 Orbit Study Demonstrating Sustained Reductions in Fracture Rates Following Treatment with Setrusumab (UX143) in Patients with Osteogenesis Imperfecta (OI)
        Jun 11 KRYS Krystal Biotech Stock Sees RS Rating Jump To 91
        Jun 11 NGNE Neurogene a new outperform at Baird on gene therapy for Rett syndrome
        Jun 10 KRYS ICC Holdings, Diamond Offshore Drilling, CrowdStrike And Other Big Stocks Moving Higher On Monday
        Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
        Related Stock Lists: Biopharmaceutical Cancer Medicine Organ Systems Antisense RNA Biotechnology Disorders Drug Discovery Drugs Dystrophy Enzyme Replacement Therapy Inborn Errors Of Metabolism Infectious Diseases Influenza Life Sciences Lipid Lipid Storage Disorders Lysosomal Storage Disorder Orphan Drug Pompe Disease
        Rare Diseases

        Rare diseases are medical conditions that affect a small percentage of the population. They are often genetic, chronic, and progressive, and can cause significant physical and mental disability. There are over 7,000 rare diseases, and many of them have no known cure.

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