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    Rare Genetic Disease Stocks List

    Symbol Grade Name % Change
    BPMC C Blueprint Medicines Corporation 2.26
    SYBX F Synlogic, Inc. -3.10
    BDTX F Black Diamond Therapeutics, Inc. -1.03
    INZY F Inozyme Pharma, Inc. -2.51
    ADVM F Adverum Biotechnologies, Inc. -4.05
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    Related Industries: Biotechnology
    Related Stock Lists: Genetic Diseases Rare Genetic Diseases Cancer Disease Biology Biopharmaceutical Biotechnology Tyrosine Kinase Receptors Adverum Biotechnologies Black Diamond Cancer Treatment Cell Biology Cell Signaling Diabetes Diamond Enzymes Epidermal Growth Factor Receptor Fibroblast Growth Factor Receptor Gastrointestinal Gastrointestinal Stromal Tumor

    Related ETFs - A few ETFs which own one or more of the above listed Rare Genetic Disease stocks.

    Symbol Grade Name Weight
    CANC D Tema Oncology ETF 4.05
    PBE D PowerShares Dynamic Biotech & Genome 2.91
    WDNA D WisdomTree BioRevolution Fund 2.44
    XBI D SPDR S&P Biotech ETF 1.69
    CNCR F Loncar Cancer Immunotherapy ETF 1.58
    View all Rare Genetic Disease ETFs...
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    Compare CANC to PBE Compare PBE to CNCR Compare WDNA to XBI

        Rare Genetic Disease Stocks Recent News

        Date Stock Title
        Nov 20 ADVM Adverum Biotechnologies Reports Inducement Grant Under Nasdaq Listing Rule 5635(c)(4)
        Nov 18 ADVM Adverum: Ixo-Vec Could Reduce Treatment Burden For Wet-AMD Patients
        Nov 18 ADVM Adverum Reports Positive Ixo-vec Data for Wet Age-Related Macular Degeneration; Shares Rise Pre-Bell
        Nov 18 ADVM Adverum Biotechnologies Announces Positive 52-Week LUNA and 4-Year OPTIC Results, and Provides Key Pivotal Program Design Elements
        Nov 15 BPMC Blueprint Medicines' Growth With AYVAKIT And Next-Gen Oncology Drugs
        Nov 15 ADVM Adverum Biotechnologies Announces Webcast to Report 52-Week LUNA Phase 2 Clinical Data and 4-Year OPTIC Clinical Data, and to Provide Key Pivotal Program Design Elements
        Nov 15 SYBX Synlogic Third Quarter 2024 Earnings: US$0.01 loss per share (vs US$2.57 loss in 3Q 2023)
        Nov 14 BPMC Blood Cancer-Focused Blueprint Medicines Could Be 'Attractive Target For Partnerships': Analyst
        Related Industries: Biotechnology
        Related Stock Lists: Genetic Diseases Rare Genetic Diseases Cancer Disease Biology Biopharmaceutical Biotechnology Tyrosine Kinase Receptors Adverum Biotechnologies Black Diamond Cancer Treatment Cell Biology Cell Signaling Diabetes Diamond Enzymes Epidermal Growth Factor Receptor Fibroblast Growth Factor Receptor Gastrointestinal Gastrointestinal Stromal Tumor
        Rare Genetic Disease

        Rare genetic diseases are genetic disorders that are present in a very small percentage of the population. These diseases are caused by mutations in a single gene or a combination of genes, and can be inherited from a parent or occur spontaneously. Symptoms of rare genetic diseases can vary widely, and can range from mild to severe. Treatment options for rare genetic diseases are often limited, and may include medications, lifestyle changes, and surgery.

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