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    Rare Diseases Stocks List

    Symbol Grade Name % Change
    SWTX F SpringWorks Therapeutics, Inc. 0.94
    ZVRA F Zevra Therapeutics, Inc. 2.00
    KROS F Keros Therapeutics, Inc. -1.79
    CYTH F Cyclo Therapeutics, Inc. -0.85
    CNTG F Centogene N.V. 1.01
    AURA F Aura Biosciences, Inc. -4.22
    PASG F Passage Bio, Inc. 0.22
    ABEO F Abeona Therapeutics Inc. -2.99
    INM F InMed Pharmaceuticals Inc. -6.35
    TAK F Takeda Pharmaceutical Company Limited 0.78
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    Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
    Related Stock Lists: Biopharmaceutical Biotechnology Clinical Development Drug Discovery Gene Therapy Medicine Organ Systems Antisense RNA Cancer Cardiomyopathy Clinical Research Dystrophy Genetic Diseases Therapeutic Gene Modulation Achondroplasia Acquired Hemolytic Anemia Acromegaly Alcohol Alport Syndrome Amyloid

    Related ETFs - A few ETFs which own one or more of the above listed Rare Diseases stocks.

    Symbol Grade Name Weight
    PINK A Simplify Health Care ETF 10.91
    PBE B PowerShares Dynamic Biotech & Genome 8.56
    HELX B Franklin Genomic Advancements ETF 7.93
    GNOM B Global X Genomics & Biotechnology ETF 7.21
    BBP B BioShares Biotechnology Products Fund 6.35
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        Rare Diseases Stocks Recent News

        Date Stock Title
        Jun 25 KROS Analyst Sees Keros Therapeutics As Next Acceleron, Set For Major Biotech Growth
        Jun 25 CYTH Cyclo Therapeutics to Present at the Society for the Study of Inborn Errors of Metabolism (SSIEM) Annual Symposium 2024
        Jun 25 TAK Wave jumps on trial data for Huntington’s disease therapy
        Jun 25 ZVRA Zevra Therapeutics Expands Executive Leadership Team
        Jun 24 TAK Takeda gets Japan nod for first post-transplant anti-CMV treatment
        Jun 24 TAK FDA Expands argenx's (ARGX) Vyvgart Label to Treat Rare Disorder
        Jun 24 TAK Takeda reports positive data from Phase IIb trial of ITP treatment
        Jun 24 TAK EC approves Takeda’s Fruzaqla for metastatic colorectal cancer
        Jun 24 TAK Takeda Announces Approval of LIVTENCITY® (maribavir) in Japan for Post-Transplant Cytomegalovirus (CMV) Infection/Disease That Is Refractory to Existing Anti-CMV Therapies
        Jun 23 TAK Takeda Presents Late-Breaking Data from Phase 2b Study of Mezagitamab, Demonstrating Potential to Transform Treatment of Primary Immune Thrombocytopenia
        Jun 21 TAK Takeda gets EU approval for Fruzaqla for colorectal cancer
        Jun 21 TAK HUTCHMED Announces European Commission Approval for FRUZAQLA® (fruquintinib) Received by Takeda
        Jun 21 TAK Takeda Receives Approval from European Commission for FRUZAQLA in Previously Treated Metastatic Colorectal Cancer
        Jun 21 TAK Takeda's HyQvia® Approved as Replacement Therapy for Primary Humoral Immunodeficiency and Secondary Humoral Immunodeficiency in Pediatric Patients 2 years of Age and Older
        Jun 21 ABEO Insider Sale: Director Christine Silverstein Sells Shares of Abeona Therapeutics Inc (ABEO)
        Jun 19 ZVRA Breakeven On The Horizon For Zevra Therapeutics, Inc. (NASDAQ:ZVRA)
        Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
        Related Stock Lists: Biopharmaceutical Biotechnology Clinical Development Drug Discovery Gene Therapy Medicine Organ Systems Antisense RNA Cancer Cardiomyopathy Clinical Research Dystrophy Genetic Diseases Therapeutic Gene Modulation Achondroplasia Acquired Hemolytic Anemia Acromegaly Alcohol Alport Syndrome Amyloid
        Rare Diseases

        Rare diseases are medical conditions that affect a small percentage of the population. They are often genetic, chronic, and progressive, and can cause significant physical and mental disability. There are over 7,000 rare diseases, and many of them have no known cure.

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