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    Rare Diseases Stocks List

    Symbol Grade Name % Change
    ABEO F Abeona Therapeutics Inc. 10.95
    AKTX F Akari Therapeutics Plc 0.00
    ALDX D Aldeyra Therapeutics, Inc. 2.86
    AURA F Aura Biosciences, Inc. -1.33
    AVRO D AVROBIO, Inc. 2.56
    AZTR F Azitra Inc. 0.34
    BLUE F bluebird bio, Inc. 1.87
    BMRN F BioMarin Pharmaceutical Inc. 1.21
    BOLD F Boundless Bio, Inc. 4.31
    CNTG F Centogene N.V. -0.02
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    Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
    Related Stock Lists: Biotechnology Myotonic Dystrophy Applied Genetics Cancer Dermatology Disorders Gene Therapy Genodermatoses Lipid Medicine Molecular Biology Neurological Disorders Ocular Disease Organ Systems Pharmaceutical Acid Acromegaly Alcohol Alport Syndrome Alzheimer's Disease

    Related ETFs - A few ETFs which own one or more of the above listed Rare Diseases stocks.

    Symbol Grade Name Weight
    GNOM C Global X Genomics & Biotechnology ETF 12.42
    LABD F Direxion Daily S&P Biotech Bear 3X Shares 9.93
    BBP C BioShares Biotechnology Products Fund 9.9
    PINK D Simplify Health Care ETF 9.67
    PBE B PowerShares Dynamic Biotech & Genome 8.9
    View all Rare Diseases ETFs...
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        Rare Diseases Stocks Recent News

        Date Stock Title
        May 15 BMRN BioMarin: Short-Term Headwinds But Long-Term Opportunities Remain
        May 15 ABEO Abeona Therapeutics GAAP EPS of -$1.16 misses by $0.65
        May 15 ABEO Abeona Therapeutics Reports First Quarter 2024 Financial Results and Recent Corporate Progress
        May 14 BMRN BioMarin Pharmaceutical to lay off 170 employees
        May 14 BMRN Evercore says biotech ‘winter is finally thawing’
        May 14 ALDX Is Aldeyra Therapeutics (ALDX) Stock Outpacing Its Medical Peers This Year?
        May 14 CNTG CENTOGENE and Evotec Discover Promising New Molecule to Treat Gaucher Disease
        May 13 BOLD Boundless Bio GAAP EPS of -$12.27 misses by $11.54
        May 13 BOLD Boundless Bio Reports First Quarter 2024 Financial Results and Corporate Highlights
        May 11 BLUE bluebird bio, Inc. (BLUE) Q1 2024 Earnings Call Transcript
        May 10 BLUE bluebird bio Inc (BLUE) Q1 2024 Earnings: Surpasses Revenue Expectations with Strategic Focus ...
        May 10 BLUE bluebird (BLUE) Tops on Q1 Sales, Zynteglo Progresses Well
        May 10 AZTR Azitra GAAP EPS of -$0.15
        May 10 AZTR Azitra, Inc. Announces Positive Preclinical Data of ATR-12 and Clinical Design in Netherton Syndrome Presented at the ASGCT Annual Meeting
        May 10 CNTG CENTOGENE Biodatabank Grows to Incorporate Disease Insights From Over 850,000 Diverse Patients
        May 9 AZTR Azitra, Inc. Announces Q1 2024 Financial Results and Provides Business Updates
        May 9 BLUE Bluebird bio spikes even as CRISPR leads in gene therapy rollout
        May 9 BMRN (BMRN) - Analyzing Biomarin Pharmaceutical's Short Interest
        May 9 BLUE bluebird bio reports Q1 results
        May 9 BLUE bluebird bio Reports First Quarter 2024 Results and Highlights Operational Progress and 2024 Guidance
        Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
        Related Stock Lists: Medicine Biopharmaceutical Biotechnology Cancer Dystrophy Enzyme Replacement Therapy Organ Systems Acid Antisense RNA Autoimmune Disease Drug Discovery Inborn Errors Of Metabolism Infectious Diseases Influenza Life Sciences Lysosomal Storage Disorder Medical Genetics Mucopolysaccharidosis Myopathy Orphan Drug
        Rare Diseases

        Rare diseases are medical conditions that affect a small percentage of the population. They are often genetic, chronic, and progressive, and can cause significant physical and mental disability. There are over 7,000 rare diseases, and many of them have no known cure.

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