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    Rare Diseases Stocks List

    Symbol Grade Name % Change
    GSK A GlaxoSmithKline PLC 0.35
    WVE C WAVE Life Sciences Ltd. 0.51
    DSGN C Design Therapeutics, Inc. 1.34
    SRPT C Sarepta Therapeutics, Inc. 0.90
    DNTH C Dianthus Therapeutics, Inc. -0.21
    LIFE C aTyr Pharma, Inc. 3.65
    LRMR D Larimar Therapeutics, Inc. 0.00
    GBIO D Generation Bio Co. 11.86
    PASG D Passage Bio, Inc. -4.15
    ALDX D Aldeyra Therapeutics, Inc. 2.86
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    Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
    Related Stock Lists: Biotechnology Biopharmaceutical Life Sciences Cancer Dystrophy Pharmacy Acid Genetic Genealogy Medical Genetics Muscular Dystrophy Myopathy Alzheimer's Disease Amphetamine Amyotrophic Lateral Sclerosis Arcturus Therapeutics Attention Deficit Hyperactivity Disorder Biologics Biology Cancer Center Childhood

    Related ETFs - A few ETFs which own one or more of the above listed Rare Diseases stocks.

    Symbol Grade Name Weight
    GNOM C Global X Genomics & Biotechnology ETF 12.42
    LABD F Direxion Daily S&P Biotech Bear 3X Shares 9.93
    BBP C BioShares Biotechnology Products Fund 9.9
    PINK D Simplify Health Care ETF 9.67
    PBE B PowerShares Dynamic Biotech & Genome 8.9
    View all Rare Diseases ETFs...
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        Rare Diseases Stocks Recent News

        Date Stock Title
        May 15 GSK GSK PLC's Dividend Analysis
        May 15 LIFE aTyr Pharma to Present Poster Describing Efzofitimod’s Mechanism of Action at the American Thoracic Society 2024 International Conference
        May 14 ALDX Is Aldeyra Therapeutics (ALDX) Stock Outpacing Its Medical Peers This Year?
        May 14 SRPT Sarepta upgraded at Oppenheimer on potential Elevidys label expansion
        May 14 LIFE aTyr Pharma Announces Second Positive DSMB Review for Efzofitimod in Phase 3 EFZO-FIT™ Study in Pulmonary Sarcoidosis
        May 13 GBIO Generation Bio GAAP EPS of -$1.12 misses by $0.71, revenue of $4.1M beats by $2.73M
        May 13 GBIO Generation Bio Co. (GBIO) Reports Q1 Loss, Tops Revenue Estimates
        May 13 GBIO Generation Bio Announces Recent Business Highlights and First Quarter 2024 Financial Results
        May 13 GSK Amazon Pours ~$1.3B Investment Into French Operations: Report
        May 12 WVE Wave Life Sciences Ltd. (NASDAQ:WVE) Just Reported First-Quarter Earnings And Analysts Are Lifting Their Estimates
        May 11 GSK GSK plc (LON:GSK) Stock Goes Ex-Dividend In Just Four Days
        May 10 WVE Wave Life Sciences Ltd. (NASDAQ:WVE) Q1 2024 Earnings Call Transcript
        May 10 DSGN Design Therapeutics Inc (DSGN) Q1 2024 Earnings: A Detailed Financial and Strategic Review
        May 10 WVE WAVE Life Sciences Reports First Quarter 2024 Financial Results
        May 10 WVE Wave Life Sciences First Quarter 2024 Earnings: US$0.24 loss per share (vs US$0.27 loss in 1Q 2023)
        May 10 LRMR Companies Like Larimar Therapeutics (NASDAQ:LRMR) Are In A Position To Invest In Growth
        May 9 SRPT HHS panel to vote in Nov. on DMD screening for newborns
        May 9 DNTH Dianthus Therapeutics GAAP EPS of -$0.54 misses by $0.10, revenue of $0.87M beats by $0.5M
        May 9 LRMR Larimar Therapeutics files for $300M mixed shelf offering
        May 9 DNTH Dianthus Therapeutics Highlights Recent Business Achievements and Reports Q1 Financial Results
        Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
        Related Stock Lists: Medicine Biopharmaceutical Biotechnology Cancer Dystrophy Enzyme Replacement Therapy Organ Systems Acid Antisense RNA Autoimmune Disease Drug Discovery Inborn Errors Of Metabolism Infectious Diseases Influenza Life Sciences Lysosomal Storage Disorder Medical Genetics Mucopolysaccharidosis Myopathy Orphan Drug
        Rare Diseases

        Rare diseases are medical conditions that affect a small percentage of the population. They are often genetic, chronic, and progressive, and can cause significant physical and mental disability. There are over 7,000 rare diseases, and many of them have no known cure.

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