or Try an Advanced Search...

    Rare Diseases Stocks List

    Symbol Grade Name % Change
    AVRO D AVROBIO, Inc. 2.52
    ABEO F Abeona Therapeutics Inc. -5.56
    AKTX F Akari Therapeutics Plc 10.39
    ALDX B Aldeyra Therapeutics, Inc. 6.60
    FOLD D Amicus Therapeutics, Inc. 4.40
    TARA D ArTara Therapeutics, Inc. -1.68
    AURA D Aura Biosciences, Inc. 3.38
    RCEL F Avita Medical Limited 2.98
    AZTR D Azitra Inc. 1.22
    BMRN D BioMarin Pharmaceutical Inc. 3.18
    View As Page of Charts
    Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
    Related Stock Lists: Biotechnology Medicine Biopharmaceutical Cancer Autoimmune Disease Biology Enzyme Replacement Therapy Gene Therapy Genetic Engineering Genodermatoses Inborn Errors Of Metabolism Life Sciences Lysosomal Storage Disorder Molecular Biology Organ Systems Pompe Disease Virotherapy Achondroplasia Acquired Hemolytic Anemia Adeno Associated Virus

    Related ETFs - A few ETFs which own one or more of the above listed Rare Diseases stocks.

    Symbol Grade Name Weight
    PINK B Simplify Health Care ETF 8.61
    GNOM D Global X Genomics & Biotechnology ETF 8.32
    IDNA C iShares Genomics Immunology and Healthcare ETF 5.83
    PBE C PowerShares Dynamic Biotech & Genome 5.43
    LABD C Direxion Daily S&P Biotech Bear 3X Shares 5.42
    View all Rare Diseases ETFs...
    Compare ETFs
    Compare GNOM to IDNA Compare PINK to GNOM Compare PINK to LABD

        Rare Diseases Stocks Recent News

        Date Stock Title
        May 1 AKTX Akari gains despite leadership change amid portfolio shakeup
        May 1 FOLD Will Amicus Therapeutics (FOLD) Report Negative Q1 Earnings? What You Should Know
        May 1 AKTX Samir R. Patel, M.D. Appointed Interim CEO for Akari Therapeutics
        May 1 AKTX Akari Therapeutics and Peak Bio Announce Portfolio Prioritization Plan for Combined Go-Forward Merger Entity
        May 1 FOLD Amicus Therapeutics to Announce First Quarter 2024 Financial Results on May 9, 2024
        Apr 30 BMRN BioMarin Pharmaceutical Inc. Beat Analyst Estimates: See What The Consensus Is Forecasting For This Year
        Apr 29 BMRN BioMarin Pharmaceutical Investors Overfocused on Roctavian, Distracted From Enzyme Replacement Therapies, UBS Says
        Apr 27 BMRN 4 Dominant Growth Stocks You'll Regret Not Buying in the New Nasdaq Bull Market
        Apr 27 BMRN Beyond the Balance Sheet: What SWOT Reveals About Biomarin Pharmaceutical Inc (BMRN)
        Apr 26 BMRN BioMarin Pharmaceutical Inc. (NASDAQ:BMRN) Q1 2024 Earnings Call Transcript
        Apr 26 BMRN BioMarin Pharmaceutical First Quarter 2024 Earnings: EPS Beats Expectations
        Apr 26 BMRN Pfizer hemophilia gene therapy arrives in US to uncertain future
        Apr 25 BMRN Why Caterpillar Shares Are Trading Lower By Around 7%? Here Are Other Stocks Moving In Thursday's Mid-Day Session
        Apr 25 BMRN BioMarin (BMRN) Beats on Q1 Earnings, Voxzogo Drives Sales
        Apr 25 BMRN BioMarin drops drug programs in pipeline cull
        Apr 25 ABEO ABEO: Receives CRL Based on Need for More CMC Information…
        Apr 25 ALDX Aldeyra Therapeutics Highlights Recent Preclinical Data in Obesity, Atopic Dermatitis, Pain, and Alcoholic Hepatitis, and Announces Planned Pivotal Clinical Trial in Retinitis Pigmentosa, at 2024 Research & Development Day
        Apr 25 BMRN Q1 2024 Biomarin Pharmaceutical Inc Earnings Call
        Apr 25 BMRN 3 Biotech Stocks That Could Be Multibaggers in the Making: April Edition
        Apr 25 BMRN Biomarin Pharmaceutical Inc (BMRN) Q1 2024 Earnings Call Transcript Highlights: Strong Growth ...
        Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
        Related Stock Lists: Biopharmaceutical Biotechnology Life Sciences Medicine Cancer Organ Systems Clinical Development Clinical Research Infectious Diseases Influenza Acid Angioedema Antacid Antibiotics Antisense RNA Asthma Ataxia Autoimmune Disease Biology Body Care Products
        Rare Diseases

        Rare diseases are medical conditions that affect a small percentage of the population. They are often genetic, chronic, and progressive, and can cause significant physical and mental disability. There are over 7,000 rare diseases, and many of them have no known cure.

        Browse All Tags