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    Rare Diseases Stocks List

    Symbol Grade Name % Change
    GSK A GlaxoSmithKline PLC 0.35
    SRPT B Sarepta Therapeutics, Inc. 2.32
    DSGN B Design Therapeutics, Inc. 1.92
    WVE C WAVE Life Sciences Ltd. 4.42
    DNTH C Dianthus Therapeutics, Inc. 7.46
    MREO C Mereo BioPharma Group plc 4.82
    CYTH C Cyclo Therapeutics, Inc. 2.72
    ALDX C Aldeyra Therapeutics, Inc. -1.19
    PULM C Pulmatrix, Inc. -3.44
    KRYS D Krystal Biotech, Inc. 0.54
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    Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
    Related Stock Lists: Biotechnology Life Sciences Biopharmaceutical Gene Therapy Applied Genetics Biology Cancer Disease Metabolic Disorders Molecular Biology Acid Alzheimer's Disease Amphetamine Amyotrophic Lateral Sclerosis Angioedema Ataxia Attention Deficit Hyperactivity Disorder Biologics Biotherapeutic Products Cardiomyopathy

    Related ETFs - A few ETFs which own one or more of the above listed Rare Diseases stocks.

    Symbol Grade Name Weight
    LABD D Direxion Daily S&P Biotech Bear 3X Shares 1.87
    BIS D ProShares UltraShort Nasdaq Biotechnology 0.65
    BBP D BioShares Biotechnology Products Fund 0.58
    MOON D Direxion Moonshot Innovators ETF 0.46
    GNOM D Global X Genomics & Biotechnology ETF 0.2
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    Compare BIS to BBP Compare BIS to MOON Compare LABD to BIS

        Rare Diseases Stocks Recent News

        Date Stock Title
        May 3 KRYS Krystal Biotech Q1 2024 Earnings Preview
        May 3 SRPT Gene Therapy Pioneer Jerry R. Mendell, M.D., Named to Inaugural TIME100 Health List of the 100 Most Influential People in Global Health
        May 3 KRYS Why Krystal Biotech (KRYS) Might Surprise This Earnings Season
        May 2 SRPT Sarepta Therapeutics to Benefit as Regulatory Review on DMD Therapy Picks Up, Morgan Stanley Says
        May 2 SRPT Sarepta Elevidys accelerated approval criticized by ICER exec
        May 2 SRPT Sarepta (SRPT) Q1 Earnings Beat Estimates, Revenues Up Y/Y
        May 2 SRPT Sarepta Therapeutics, Inc. (NASDAQ:SRPT) Q1 2024 Earnings Call Transcript
        May 2 WVE Wave Life Sciences First Quarter 2024 Financial Results Scheduled for May 9, 2024
        May 2 KRYS Krystal Biotech to Present at the Association for Research in Vision and Ophthalmology 2024 Annual Meeting
        May 2 SRPT Q1 2024 Sarepta Therapeutics Inc Earnings Call
        May 2 SRPT Sarepta Therapeutics Inc (SRPT) Q1 2024 Earnings Call Transcript Highlights: Robust Revenue ...
        May 2 GSK GSK First Quarter 2024 Earnings: Revenues Beat Expectations, EPS Lags
        May 1 SRPT Sarepta Therapeutics (SRPT) Q1 Earnings: Taking a Look at Key Metrics Versus Estimates
        May 1 SRPT Sarepta Therapeutics (SRPT) Q1 2024 Earnings Call Transcript
        May 1 SRPT Sarepta Therapeutics, Inc. (SRPT) Q1 2024 Earnings Call Transcript
        May 1 SRPT Sarepta Therapeutics (SRPT) Q1 Earnings and Revenues Beat Estimates
        May 1 SRPT Sarepta Therapeutics jumps 5% on Q1 beats
        May 1 SRPT Sarepta Therapeutics Non-GAAP EPS of $0.73 beats by $0.43, revenue of $413.5M beats by $43.02M
        May 1 SRPT Sarepta Therapeutics Announces First Quarter 2024 Financial Results and Recent Corporate Developments
        May 1 GSK GSK Sees Strong Demand For Vaccines and Asthma Drugs, Raises Annual Outlook
        Related Industries: Biotechnology Diagnostics & Research Drug Manufacturers - Major Drug Manufacturers - Specialty & Generic Medical Devices
        Related Stock Lists: Biotechnology Childhood Dystrophy Genetic Genealogy Human Diseases Iglo Medical Genetics Medicine Oncology Diseases Sickle Cell Disease Summit Thalassemia
        Rare Diseases

        Rare diseases are medical conditions that affect a small percentage of the population. They are often genetic, chronic, and progressive, and can cause significant physical and mental disability. There are over 7,000 rare diseases, and many of them have no known cure.

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